CRUSH RETT SYNDROME
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Mission Statement
Crush Rett Syndrome's mission is to raise funds and awareness to treat and ultimately cure Rett Syndrome.Two human gene therapy clinical trials are being conducted with the first patient dosed in Q2 2023! Positive results have supported the continuation of the Phase 1/2 trial.
About This Cause
Crush Rett Syndrome's mission is to raise funds and awareness to treat and ultimately cure Rett Syndrome. Rett Syndrome is a non-degenerative neurological disorder that affects over 350,000 mostly females worldwide. Symptoms do not typically appear until between 6 to 18 months when most acquired skills are lost. Seizures, severe scoliosis, tremors, irregular breathing and heart rhythms are common. The hallmark symptoms of Rett Syndrome is the loss of purposeful hand use and the inability to speak, replacing them with constant hand-wringing and hand-mouthing with limited ability to communicate. The gene responsible for Rett Syndrome has been found. Research has shown that a cure can reverse the symptoms giving Rett Syndrome sufferers a second chance at a normal life. In addition, enormous progress has been made in understanding the role of the Rett Syndrome gene which in turn has uncovered the role of other genes and proteins that cause similar symptoms in Parkinson's, Alzheimers, Autism, Schizophrenia, and Traumatic Brain Injuries. Giving to Crush Rett Syndrome not only helps those with Rett Syndrome but also research for many other neurological disorders.